Safety and efficacy of subretinal readministration of a viral vector in large animals to treat congenital blindness.

Author List
Amado D, Mingozzi F, Hui D, Bennicelli JL, Wei Z, Chen Y, Bote E, Grant RL, Golden JA, Narfstrom K, Syed NA, Orlin SE, High KA, Maguire AM, Bennett J
Publication ID (Profile URL)
https://researcherprofiles.org/profile/7165910
Publication Year
2010
PubMed ID
20374996
Publication Title
Amado D, Mingozzi F, Hui D, Bennicelli JL, Wei Z, Chen Y, Bote E, Grant RL, Golden JA, Narfstrom K, Syed NA, Orlin SE, High KA, Maguire AM, Bennett J. Safety and efficacy of subretinal readministration of a viral vector in large animals to treat congenital blindness. Sci Transl Med. 2010 Mar 03; 2(21):21ra16.