Identification of a robust promoter in mouse and human hepatocytes by in vivo biopanning of a barcoded AAV library. Read more about Identification of a robust promoter in mouse and human hepatocytes by in vivo biopanning of a barcoded AAV library.
A platform to deliver single and bi-specific Cas9/guide RNA to perturb genes in vitro and in vivo. Read more about A platform to deliver single and bi-specific Cas9/guide RNA to perturb genes in vitro and in vivo.
In vivo selection of anti-HIV-1 gene-modified human hematopoietic stem/progenitor cells to enhance engraftment and HIV-1 inhibition. Read more about In vivo selection of anti-HIV-1 gene-modified human hematopoietic stem/progenitor cells to enhance engraftment and HIV-1 inhibition.
Potential clinical use of azacitidine and MEK inhibitor combination therapy in PTPN11-mutated juvenile myelomonocytic leukemia. Read more about Potential clinical use of azacitidine and MEK inhibitor combination therapy in PTPN11-mutated juvenile myelomonocytic leukemia.
Transient expression of factor VIII and a chronic high-fat diet induces ER stress and late hepatocyte oncogenesis. Read more about Transient expression of factor VIII and a chronic high-fat diet induces ER stress and late hepatocyte oncogenesis.
Inhibition of BTK and PI3Kδ impairs the development of human JMML stem and progenitor cells. Read more about Inhibition of BTK and PI3Kδ impairs the development of human JMML stem and progenitor cells.
Dual Targeting of Mesothelin and CD19 with Chimeric Antigen Receptor-Modified T Cells in Patients with Metastatic Pancreatic Cancer. Read more about Dual Targeting of Mesothelin and CD19 with Chimeric Antigen Receptor-Modified T Cells in Patients with Metastatic Pancreatic Cancer.
Aberrant Clonal Hematopoiesis following Lentiviral Vector Transduction of HSPCs in a Rhesus Macaque. Read more about Aberrant Clonal Hematopoiesis following Lentiviral Vector Transduction of HSPCs in a Rhesus Macaque.
Low-Dose Radiation Conditioning Enables CAR T Cells to Mitigate Antigen Escape. Read more about Low-Dose Radiation Conditioning Enables CAR T Cells to Mitigate Antigen Escape.
Age-Related Impaired Efficacy of Bone Marrow Cell Therapy for Myocardial Infarction Reflects a Decrease in B Lymphocytes. Read more about Age-Related Impaired Efficacy of Bone Marrow Cell Therapy for Myocardial Infarction Reflects a Decrease in B Lymphocytes.